Mitochondrial Medicine – Therapeutic Development (Virtual Conference)

Artistic representation of mitochondria cells
30 November, 2021 - 2 December, 2021

General Information

Owing to the ongoing situation with covid-19, this Wellcome Connecting Science conference will be organised as a virtually.

Mitochondrial disorders have emerged as a major cause of inherited human disease. Although the past decade has seen major advances in our understanding of their genetic basis and the underlying pathology, these findings have yet to translate into new therapies. There is a growing appreciation that new treatments will only emerge through a concerted collaboration between clinicians, laboratory scientists and the life sciences industry, based on a firm understanding of the disease mechanisms.

This conference will build new partnerships that harness our understanding of the disease mechanisms, accelerating the pace of effective treatments for mitochondrial diseases. This year’s meeting will include pre-clinical models for mitochondrial disease, an update on validation and outcome measures for clinical trials, a discussion on the importance on data sharing for precision medicine, and guidance on regulations for therapeutic development from a range of international agencies.

We will bring together leaders in the field of translational mitochondrial medicine, with a programme designed to engage and inspire the next generation of mitochondrial researchers. The meeting attracts international participants interested in mitochondrial diseases, working in molecular genetics, biochemistry, pathology, and clinical medicine.

  • Topics will include:
    Mitochondrial medicine: pharma and funding perspectives
  • Pre-clinical mitochondrial disease models
  • Therapeutic development in mitochondrial eye diseases
  • Clinical trials – validation and outcome measures
  • Collaboration and data sharing to support precision medicine

For more information and to register, visit the event website.

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